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What is the BALANCE study?

The purpose of the BALANCE study is to determine if a potential new antisense treatment, or “investigational antisense drug,” is safe and effective in breaking down dietary fat that can lower triglycerides in the blood and potentially help improve a patient’s quality of life for people living with FCS.

  • Familial Chylomicronemia Syndrome (FCS) is a genetic, life-threatening disease, in which the patient is unable to digest fats, which often results in high triglycerides (TGs). Sustained high TG levels can lead to pancreatitis.
  • The investigational antisense drug (or placebo) will be randomly administered via subcutaneous injection beneath the skin. The Familial Chylomicronemia Syndrome (FCS) treatment is designed to target and reduce the activity of a protein in the body. Targeting this protein may help break down dietary fat and triglycerides.