Hereditary Transthyretin-Mediated Amyloid Polyneuropathy

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NEURO-TTRansform: A Study to Evaluate the Efficacy and Safety of AKCEA-TTR-LRx in Participants With Hereditary Transthyretin-Mediated Amyloid Polyneuropathy

Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM)

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CARDIO-TTRansform: A Study to Evaluate the Efficacy and Safety of AKCEA-TTR-LRx in Participants With Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM)

Macular Degeneration

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GOLDEN STUDY: A Study to Assess Safety and Efficacy of Multiple Doses of IONIS-FB-LRx in Participants With Geographic Atrophy Secondary to Age-Related Macular Degeneration (AMD)

Familial Chylomicronemia Syndrome

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A Study of AKCEA-APOCIII-LRx Administered to Patients With Familial Chylomicronemia Syndrome (FCS)

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Therapeutic Conditions

Cardio-Renal
Metabolic
Neurological
Cancer
Ophthalmology
Pulmonology and Allergy
Hematology
Other
 

Upcoming Clinical Studies

Chronic Heart Failure With Reduced Ejection Fraction

A Study to Assess the Safety, Tolerability and Efficacy of IONIS-AGT-LRx in Participants With Chronic Heart Failure With Reduced Ejection Fraction

Amyotrophic Lateral Sclerosis

A Study to Evaluate the Efficacy, Safety, Pharmacokinetics and Pharmacodynamics of ION363 in Amyotrophic Lateral Sclerosis Participants With Fused in Sarcoma Mutations (FUS-ALS)

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