Hereditary Transthyretin-Mediated Amyloid Polyneuropathy

clinical study logo

NEURO-TTRansform: A Study to Evaluate the Efficacy and Safety of AKCEA-TTR-LRx in Participants With Hereditary Transthyretin-Mediated Amyloid Polyneuropathy

Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM)

clinical study logo

CARDIO-TTRansform: A Study to Evaluate the Efficacy and Safety of AKCEA-TTR-LRx in Participants With Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM)

Macular Degeneration

clinical study logo

GOLDEN STUDY: A Study to Assess Safety and Efficacy of Multiple Doses of IONIS-FB-LRx in Participants With Geographic Atrophy Secondary to Age-Related Macular Degeneration (AMD)

Familial Chylomicronemia Syndrome

clinical study logo

A Study of AKCEA-APOCIII-LRx Administered to Patients With Familial Chylomicronemia Syndrome (FCS)

Search for a Study icon-slider

 

Hide Tools »

Therapeutic Conditions

Cardio-Renal
Metabolic
Neurological
Cancer
Ophthalmology
Pulmonology and Allergy
Hematology
Other
 

Upcoming Clinical Studies


Working with our Community

Through our collaborations with patient advocacy organizations and communities worldwide we work to identify and understand the most urgent needs of people living with severe diseases and their caregivers. As experts in living with their disease, the patient and caregiver perspectives inform our approach to research.